Muscular dystrophy can appear in infancy up to middle age or later, and its form and severity are determined in part by the age at which it occurs. Some types of muscular dystrophy typically ...

DM1 (formerly known as Steinert disease) is caused by a defect in the DMPK gene on chromosome 19 and is a form of muscular dystrophy, leading to weakness and loss of function in voluntary muscles ...

Also known as Steinert’s disease ... also developing PGN-EDO51 for patients with exon 51 amenable Duchenne muscular dystrophy. The candidate is being assessed in the Phase II CONNECT1-EDO51 ...